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Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Read our disclaimer for details.
 
ClinicalTrials.gov Identifier: NCT04201405
Recruitment Status : Active, not recruiting
First Posted : December 17, 2019
Last Update Posted : July 6, 2021
Sponsor:
Collaborators:
Orchard Therapeutics
CTI Clinical Trial and Consulting Services
University College, London
Great Ormond Street Hospital for Children NHS Foundation Trust
Manchester University NHS Foundation Trust
Information provided by (Responsible Party):
Rob Wynn, Manchester University NHS Foundation Trust

No Study Results Posted on ClinicalTrials.gov for this Study
Recruitment Status : Active, not recruiting
Estimated Primary Completion Date : October 30, 2024
Estimated Study Completion Date : October 30, 2024
Publications: