Early Access Program With Arimoclomol in US Patients With NPC
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|ClinicalTrials.gov Identifier: NCT04316637|
Expanded Access Status : Available
First Posted : March 20, 2020
Last Update Posted : October 9, 2020
|First Submitted Date||March 18, 2020|
|First Posted Date||March 20, 2020|
|Last Update Posted Date||October 9, 2020|
|Brief Title||Early Access Program With Arimoclomol in US Patients With NPC|
NPC is a rare, relentlessly progressive, neurological disease and associated with serious morbidity and shortened life expectancy.
The purpose of this Expanded Access Program is to provide early access to arimoclomol for patients with Niemann-Pick Type C disease who, in the opinion and the clinical judgement of the treating physician, may benefit from treatment with arimoclomol.
Participants will receive treatment with arimoclomol until their doctor finds it does not help them anymore, they withdraw, or the study is stopped for any reason.
|Detailed Description||Not Provided|
|Study Type||Expanded Access|
|Expanded Access Type||Intermediate-size Population|
Participants receive prescribed arimoclomol by oral administration
|Publications *||Not Provided|
* Includes publications given by the data provider as well as publications identified by ClinicalTrials.gov Identifier (NCT Number) in Medline.
|Expanded Access Status||Available|
|Listed Location Countries||United States|
|Removed Location Countries|
|Verification Date||September 2020|