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Found 134 studies with search of: Muscular Dystrophy
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Rank Status Study
1 Recruiting Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Sildenafil
2 Active, not recruiting Evaluation of Limb-Girdle Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy, Type 2A;   Calpain-3 Deficiency;   Limb-Girdle Muscular Dystrophy, Type 2B;   Miyoshi Myopathy;   Dysferlin Deficiency;   Limb-Girdle Muscular Dystrophy, Type 2I;   FKRP-deficiency
Intervention:
3 Completed Phase 2b Study of PTC124 in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: PTC124
4 Completed Gentamicin Treatment of Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Duchenne Muscular Dystrophy
Intervention: Drug: Gentamicin
5 Recruiting Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Intervention:
6 Active, not recruiting Cardiac Outcome Measures in Children With Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention:
7 Recruiting Tadalafil in Becker Muscular Dystrophy
Condition: Becker Muscular Dystrophy
Interventions: Drug: Tadalafil;   Drug: Placebo
8 Unknown  The Efficacy of Using Far Infrared Radiation to Manage Muscular Dystrophies
Condition: Muscular Dystrophies
Intervention: Radiation: Far Infrared Radiation
9 Active, not recruiting Arrhythmias in Myotonic Muscular Dystrophy
Conditions: Muscular Dystrophy;   Arrhythmia;   Sudden Cardiac Death
Intervention: Other: Screening
10 Terminated Phase 2b Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
11 Suspended Study of Ataluren (PTC124®) in Nonambulatory Patients With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
12 Recruiting Tadalafil and Sildenafil for Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: Tadalafil;   Drug: Sildenafil
13 Recruiting Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Conditions: Myotonic Dystrophy;   Muscular Dystrophy, Facioscapulohumeral;   Muscular Dystrophy
Intervention:
14 Recruiting Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention:
15 Recruiting Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy
Conditions: Muscular Dystrophies;   Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy
Intervention: Other: Retrograde high pressure transvenous perfusion with normal saline
16 Completed Cardiac Magnetic Resonance in Children With Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention:
17 Unknown  Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
Conditions: Duchenne's Muscular Dystrophy;   Scoliosis
Intervention:
18 Enrolling by invitation Follistatin Gene Transfer to Patients With Becker Muscular Dystrophy and Sporadic Inclusion Body Myositis
Conditions: Becker Muscular Dystrophy;   Sporadic Inclusion Body Myositis
Intervention: Genetic: rAAV1.CMV.huFollistatin344
19 Recruiting Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Limb Girdle Muscular Dystrophy
Intervention: Drug: Coenzyme Q10 and Lisinopril
20 Not yet recruiting Effect of Modulating the nNOS System on Cardiac, Muscular and Cognitive Function in Becker Muscular Dystrophy Patients
Condition: Becker Muscular Dystrophy
Interventions: Drug: Sildenafil;   Drug: Placebo

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