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Found 19 studies with search of: Open Studies | "Gaucher Disease"
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Rank Status Study
1 Recruiting International Collaborative Gaucher Group (ICGG) Gaucher Registry
Conditions: Gaucher Disease;   Cerebroside Lipidosis Syndrome;   Glucocerebrosidase Deficiency Disease;   Glucosylceramide Beta-Glucosidase Deficiency Disease
Intervention:
2 Recruiting Exploration of Immunity in Gaucher Disease
Condition: Gaucher Disease
Intervention:
3 Recruiting Cellular and Molecular Mechanisms Governing Bone Marrow Stem Cells in Gaucher Disease
Condition: Gaucher Disease
Intervention: Other: Bone marrow and blood sampling
4 Recruiting Thrombocytopathy in Gaucher Disease Patients
Conditions: Gaucher Disease;   Thrombocytopathy
Intervention:
5 Available Expanded Access Trial of Plant Expressed Recombinant Glucocerebrosidase (prGCD) in Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Plant cell expressed recombinant glucocerebrosidase (prGCD)
6 Recruiting Examining the Immune Response in Patients With Gaucher Disease and Hepatitis B or C
Conditions: Gaucher Disease;   Hepatitis B;   Hepatitis C
Intervention:
7 Not yet recruiting Clinical Trial of Ambroxol in Patients With Type I Gaucher Disease
Condition: Type I Gaucher Disease
Intervention: Drug: Ambroxol
8 Not yet recruiting The Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher Disease
Condition: Gaucher Disease
Interventions: Drug: Cerezyme®;   Drug: ISU302
9 Recruiting Intravenous N-acetylcysteine for the Treatment of Gaucher's Disease and Parkinson's Disease
Conditions: Parkinson's Disease;   Gaucher's Disease
Intervention: Drug: N-acetylcysteine
10 Recruiting Home Therapy With VPRIV in Gaucher's Disease
Condition: Gaucher's Disease
Intervention:
11 Unknown † Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Condition: Gaucher's Disease
Intervention: Drug: glucocerebrosidase
12 Recruiting Biomarker for Gaucher Diasease
Conditions: Lysosomal Storage Diseases;   Gaucher Disease;   Sphingolipidoses
Intervention:
13 Unknown † Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease
Conditions: Gaucher's Disease;   Osteopenia
Interventions: Drug: alendronate sodium;   Drug: calcium carbonate;   Drug: cholecalciferol
14 Recruiting Positron Emission Tomography (PET) Imaging in People With Gaucher Mutations
Conditions: Glucocerebrosidase Mutations;   Gaucher Disease
Intervention:
15 Recruiting Detecting Dopaminergic Deficits in Individuals At-risk for Parkinsonism
Conditions: Parkinson Disease;   Gaucher Disease;   Idiopathic Rapid Eye Movement Sleep Disorder
Intervention:
16 Recruiting Clinical and Basic Investigations Into Erdheim Chester Disease
Conditions: Myelofibrosis;   Gaucher Disease;   Pulmonary Fibrosis;   Hermansky-Pudlak Syndrome (HPS);   Cancer
Intervention:
17 Recruiting Nervous System Degeneration in Glycosphingolipid Storage Disorders
Conditions: Gangliosidoses;   Gaucher Disease
Intervention:
18 Recruiting Genetic Studies of Lysosomal Storage Disorders
Conditions: Gaucher's Disease;   Lysosomal Storage Disease
Intervention:
19 Recruiting MR Spectroscopy and Disease Severity Score for Gaucher in Pediatric Population
Condition: Gaucher
Intervention:

† Indicates status has not been verified in more than two years
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