Intracerebral Gene Therapy for Sanfilippo Type A Syndrome

This study is ongoing, but not recruiting participants.
Sponsor:
Information provided by (Responsible Party):
LYSOGENE
ClinicalTrials.gov Identifier:
NCT01474343
First received: November 10, 2011
Last updated: May 30, 2012
Last verified: May 2012
No Study Results Posted on ClinicalTrials.gov for this Study
  Study Status: This study is ongoing, but not recruiting participants.
  Estimated Study Completion Date: January 2014
  Estimated Primary Completion Date: January 2014 (Final data collection date for primary outcome measure)