A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I
This study is currently recruiting participants.
Verified February 2013 by Dickson, Patricia I., M.D.
Sponsor:
Patricia I. Dickson, M.D.
Collaborators:
MPS I Intrathecal Research Collaborative
The Ryan Foundation for MPS Children
BioMarin Pharmaceutical
Rare Diseases Clinical Research Network
University of Minnesota - Clinical and Translational Science Institute
University of California, Los Angeles
Information provided by (Responsible Party):
Patricia I. Dickson, M.D., Dickson, Patricia I., M.D.
ClinicalTrials.gov Identifier:
NCT00852358
First received: February 25, 2009
Last updated: February 19, 2013
Last verified: February 2013
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No Study Results Posted on ClinicalTrials.gov for this Study
| Study Status: | This study is currently recruiting participants. |
|---|---|
| Estimated Study Completion Date: | December 2018 |
| Estimated Primary Completion Date: | December 2014 (Final data collection date for primary outcome measure) |