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Trial of Kuvan in Lesch-Nyhan Disease
This study has been withdrawn prior to enrollment.
( Contractual issues )
Study NCT00935753 Information provided by University of California, San Diego
First Received on July 8, 2009. Last Updated on March 15, 2010
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Additional conditions recognized in this trial
Lesch-Nyhan Syndrome
More general conditions related to this trial
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Genetic Diseases, Inborn
Genetic Diseases, X-Linked
Heredodegenerative Disorders, Nervous System
Mental Retardation
Mental Retardation, X-Linked
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Neurobehavioral Manifestations
Neurodegenerative Diseases
Neurologic Manifestations
Purine-Pyrimidine Metabolism, Inborn Errors
Interventions listed in this trial
sapropterin
Sponsors listed in this trial
University of California, San Diego
BioMarin Pharmaceutical
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