Subcutaneous CINRYZE With Recombinant Human Hyaluronidase for Prevention of Angioedema Attacks

This study is currently recruiting participants.
Verified March 2013 by ViroPharma
Sponsor:
Collaborator:
Halozyme Therapeutics
Information provided by (Responsible Party):
ViroPharma
ClinicalTrials.gov Identifier:
NCT01756157
First received: June 29, 2012
Last updated: March 19, 2013
Last verified: March 2013
  Purpose

The primary objectives of the study are to evaluate the safety, tolerability, and efficacy of two doses of CINRYZE with recombinant human hyaluronidase (rHuPH20) administered by subcutaneous (SC) injection to prevent angioedema attacks.


Condition Intervention Phase
Hereditary Angioedema
Biological: CINRYZE with rHuPH20
Phase 2

Study Type: Interventional
Study Design: Allocation: Randomized
Endpoint Classification: Safety/Efficacy Study
Intervention Model: Crossover Assignment
Masking: Double Blind (Subject, Caregiver, Investigator, Outcomes Assessor)
Primary Purpose: Prevention
Official Title: A Phase 2, Randomized, Double-Blind, Multicenter, Dose-Ranging, Crossover Study to Evaluate the Safety and Efficacy of Subcutaneous Administration of CINRYZE® (C1 Esterase Inhibitor [Human]) With Recombinant Human Hyaluronidase (rHuPH20) for the Prevention of Angioedema Attacks in Adolescents and Adults With Hereditary Angioedema

Resource links provided by NLM:


Further study details as provided by ViroPharma:

Primary Outcome Measures:
  • Number of angioedema attacks during each randomized therapy period [ Time Frame: 8 weeks ] [ Designated as safety issue: No ]

Secondary Outcome Measures:
  • Cumulative Attack-Severity during each randomized therapy period [ Time Frame: 8 weeks ] [ Designated as safety issue: No ]
    This score is the sum of the maximum symptom severity recorded for each angioedema attack in a treatment period.


Estimated Enrollment: 40
Study Start Date: December 2012
Estimated Study Completion Date: December 2013
Estimated Primary Completion Date: November 2013 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: SC CINRYZE with rHuPH20 Dose Level 1 followed by Dose Level 2
SC CINRYZE with rHuPH20 Dose Level 1 twice weekly (every 3 or 4 days) for 8 weeks followed by SC CINRYZE with rHuPH20 Dose Level 2 twice weekly (every 3 or 4 days) for 8 weeks.
Biological: CINRYZE with rHuPH20
Other Names:
  • C1 esterase inhibitor (human)
  • Recombinant human hyaluronidase
Experimental: SC CINRYZE with rHuPH20 Dose Level 2 followed by Dose Level 1
SC CINRYZE with rHuPH20 Dose Level 2 twice weekly (every 3 or 4 days) for 8 weeks followed by SC CINRYZE with rHuPH20 Dose Level 1 twice weekly (every 3 or 4 days) for 8 weeks.
Biological: CINRYZE with rHuPH20
Other Names:
  • C1 esterase inhibitor (human)
  • Recombinant human hyaluronidase

  Eligibility

Ages Eligible for Study:   12 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion Criteria:

  • Be ≥12 years of age.
  • Have a confirmed diagnosis of Hereditary Angioedema.

Exclusion Criteria:

  • Receipt of any C1 inhibitor (C1 INH) therapy or any blood products for treatment or prevention of an angioedema attack within 7 days before the first dose of study drug.
  • Be receiving prophylactic intravenous CINRYZE that exceeds 1000 units every 3 or 4 days (maximum weekly dose 2000 units).
  • Have received any androgen therapy (e.g., danazol, oxandrolone, stanozolol, testosterone) within 7 days prior to the first dose of study drug.
  • If female, have started taking or changed the dose of any hormonal contraceptive regimen or hormone replacement therapy (i.e., estrogen/progestin containing products) within 3 months prior to the first dose of study drug.
  • History of allergic reaction to C1 INH products, including CINRYZE or other blood products.
  • History of abnormal blood clotting.
  • Have a known allergy to hyaluronidase or any other ingredient in the study formulation.
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01756157

Locations
United States, Alabama
ViroPharma Investigational Site Recruiting
Birmingham, Alabama, United States, 35209
Contact: Clincal Operations Staff     866-331-5637        
United States, California
ViroPharma Investigational Site Recruiting
Walnut Creek, California, United States, 94598
Contact: Clinical Operations Staff     866-331-5637        
United States, Colorado
ViroPharma Investigational Site Recruiting
Colorado Springs, Colorado, United States, 80907
Contact: Clinical Operations Staff     866-331-5637        
United States, Massachusetts
ViroPharma Investigational Site Recruiting
Boston, Massachusetts, United States, 02114
Contact: Clinical Operations Staff     866-331-5637        
United States, Nevada
ViroPharma Investigational Site Recruiting
Las Vegas, Nevada, United States, 89106
Contact: Clinical Operations Staff     866-331-5637        
United States, Ohio
ViroPharma Investigational Site Recruiting
Columbus, Ohio, United States, 43245
Contact: Clinical Operations Staff     866-331-5637        
United States, Oregon
ViroPharma Investigational Site Recruiting
Lake Oswego, Oregon, United States, 97035
Contact: Clinical Operations Staff     866-331-5637        
United States, Pennsylvania
Clinical Operations Staff Recruiting
Pittsburgh, Pennsylvania, United States, 15241
Contact: Clinical Operations Staff     866-331-5637        
United States, Tennessee
ViroPharma Investigational Site Recruiting
Knoxville, Tennessee, United States, 37909
Contact: Clinical Operations Staff     866-331-5637        
United States, Washington
ViroPharma Investigational Site Recruiting
Spokane, Washington, United States, 99204
Contact: Clinical Operations Staff     866-331-5637        
Germany
ViroPharma Investigational Site Recruiting
Berlin, Germany
Contact: Clinical Operations Staff     +32 2 747 09 71        
ViroPharma Investigational Site Recruiting
Essen, Germany
Contact: Clinical Operations Staff     +32 2 747 09 71        
ViroPharma Investigational Site Recruiting
Mainz, Germany
Contact: Clinical Operations Staff     +32 2 747 09 71        
ViroPharma Investigational Site Recruiting
Munchen, Germany
Contact: Clinical Operations Staff     +32 2 747 09 71        
Spain
ViroPharma Investigational Site Recruiting
Barcelona, Spain
Contact: Clinical Operations Staff     +32 2 747 09 71        
Sweden
ViroPharma Investigational Site Recruiting
Jonkoping, Sweden
Contact: Clinical Operations Staff     +32 2 747 09 71        
Sponsors and Collaborators
ViroPharma
Halozyme Therapeutics
Investigators
Study Director: Jennifer Schranz, MD ViroPharma
  More Information

No publications provided

Responsible Party: ViroPharma
ClinicalTrials.gov Identifier: NCT01756157     History of Changes
Other Study ID Numbers: 0624-206, 2012-000083-24
Study First Received: June 29, 2012
Last Updated: March 19, 2013
Health Authority: United States: Food and Drug Administration
Germany: Paul-Ehrlich-Institut
Hungary: National Institute of Pharmacy
Spain: Agencia Española de Medicamentos y Productos Sanitarios
France: Afssaps - Agence française de sécurité sanitaire des produits de santé (Saint-Denis)
Romania: National Agency for Medicines and Medical Devices
Sweden: Medical Products Agency

Keywords provided by ViroPharma:
Crossover
Prevention
Hereditary Angioedema
C1 esterase inhibitor
C1 inhibitor
Subcutaneous
Recombinant human hyaluronidase

Additional relevant MeSH terms:
Angioedema
Angioedemas, Hereditary
Vascular Diseases
Cardiovascular Diseases
Urticaria
Skin Diseases, Vascular
Skin Diseases
Hypersensitivity, Immediate
Hypersensitivity
Immune System Diseases
Genetic Diseases, Inborn
Complement C1 Inactivator Proteins
Complement C1 Inhibitor Protein
Complement C1
Complement C1s
Complement Inactivating Agents
Immunosuppressive Agents
Immunologic Factors
Physiological Effects of Drugs
Pharmacologic Actions

ClinicalTrials.gov processed this record on May 16, 2013