A Trial in Subjects Suspected to Have Tuberculosis, Comparing the Diagnostic Performance of C-Tb to QuantiFERON®, in Combination With a Safety Assessment of C-Tb Versus Tuberculin PPD RT23 SSI

This study is currently recruiting participants.
Verified January 2013 by Statens Serum Institut
Sponsor:
Information provided by (Responsible Party):
Statens Serum Institut
ClinicalTrials.gov Identifier:
NCT01642888
First received: July 5, 2012
Last updated: January 18, 2013
Last verified: January 2013
  Purpose

Tuberculosis (TB) continues to be one of the most serious bacterial infections worldwide and therefore new improved diagnostic tests are needed to help doctors in diagnosing TB.

The new skin test is named C-Tb. Like the current tuberculin skin test, PPD, the C-Tb test is injected just under the skin and will, when positive, show redness and/or swelling at the injection site while a negative test will leave no reactions. The investigators hope that this new C-Tb skin test will be more precise (specific) than the PPD test, as the PPD test e.g. may show a reaction if the person tested is BCG vaccinated.

The aim of this trial is to test the C-Tb skin test in volunteers suspected of being infected with TB.

The reasons for these tests are the following:

  • To compare the C-Tb test to a blood test, the QuantiFERON test.
  • To compare the C-Tb test to the PPD test that is currently being used.
  • To assess the safety of the C-Tb test.

Condition Intervention Phase
Tuberculosis
Biological: C-Tb
Biological: 2 T.U. Tuberculin PPD RT 23 SSI
Phase 3

Study Type: Interventional
Study Design: Allocation: Randomized
Endpoint Classification: Safety/Efficacy Study
Intervention Model: Parallel Assignment
Masking: Double Blind (Subject, Caregiver, Investigator, Outcomes Assessor)
Primary Purpose: Diagnostic
Official Title: A Phase III Trial in Subjects Suspected to Have Tuberculosis, Comparing the Diagnostic Performance of C-Tb to QuantiFERON®-TB Gold In-Tube, in Combination With a Double Blind Randomized Split Body Safety Assessment of C-Tb Versus 2 T.U. Tuberculin PPD RT23 SSI (PPD)

Resource links provided by NLM:


Further study details as provided by Statens Serum Institut:

Primary Outcome Measures:
  • The sensitivity of C-Tb compared to that of QuantiFERON®- TB Gold In Tube test [ Time Frame: Onset between the injections and 28 days after the injections ] [ Designated as safety issue: No ]

    The difference between sensitivity for C-Tb and for QuantiFERON® will be derived with a 95% confidence interval and a non-inferiority test will be performed by comparing the lower limit of the interval to a delta value of 0.15. This corresponds to testing the one-sided hypothesis H0: SensitivityC-Tb - SensitivityQF < -0.15 Against H1: SensitivityC-Tb - SensitivityQF > - 0.15

    at a 2.5% level. Rejecting the H0 corresponds to demonstrating non-inferiority of C-Tb versus QuantiFERON®.


  • The sensitivity of C-Tb compared to that of PPD [ Time Frame: From injections to 2-3 days after injections ] [ Designated as safety issue: No ]

    The endpoints sensitivity and specificity will be estimated non-linearly by finding the maximum likelihood estimates in a model describing the diagnostic outcome as a function of sensitivity, specificity and prevalence in different risk categories.

    This model will use all evaluable subjects with non-missing values for C-Tb and for PPD. Specificity will be compared as a superiority test while sensitivity will be compared with a non-inferiority limit of 0.15 as described above.


  • The specificity of C-Tb compared to that of QuantiFERON®- TB Gold In Tube test [ Time Frame: Onset between the injections and 28 days after the injections ] [ Designated as safety issue: No ]

    The difference between sensitivity for C-Tb and for QuantiFERON® will be derived with a 95% confidence interval and a non-inferiority test will be performed by comparing the lower limit of the interval to a delta value of 0.15. This corresponds to testing the one-sided hypothesis H0: SensitivityC-Tb - SensitivityQF < -0.15 Against H1: SensitivityC-Tb - SensitivityQF > - 0.15

    at a 2.5% level. Rejecting the H0 corresponds to demonstrating non-inferiority of C-Tb versus QuantiFERON®. From the same model the specificity is estimated and a similar non-inferiority test is performed.


  • The specificity of C-Tb compared to that of PPD [ Time Frame: From injections to 2-3 days after injections ] [ Designated as safety issue: No ]
    This model will use all evaluable subjects with non-missing values for C-Tb and for PPD. Specificity will be compared as a superiority test while sensitivity will be compared with a non-inferiority limit of 0.15 as described above.


Secondary Outcome Measures:
  • The diameter of induration at the C-Tb injection site measured transversely to the long axis of the forearm at 2 to 3 days after intradermal administration of C-Tb evaluated against the age and CD4 counts (HIV positive participants only) [ Time Frame: From injections to 2-3 days after the injections ] [ Designated as safety issue: No ]

    To evaluate a possible influence of age on the induration response, regression analyses will be performed separately for C-Tb and PPD. Response cut-offs will be used and only subjects with positive response will be included in the analyses. A linear, curvilinear or stepwise relationship will be used depending on the observed data. The SAP will state the final choice of cut-offs.

    A possible relationship between induration response and CD4 counts in the HIV positive sub-group will be evaluated as for the age above.


  • The diameter of induration at the PPD injection site measured transversely to the long axis of the forearm at 2 to 3 days after intradermal administration of PPD evaluated against the age and CD4 counts (HIV positive participants only) [ Time Frame: From injections to 2-3 days after the injections ] [ Designated as safety issue: No ]

    To evaluate a possible influence of age on the induration response, regression analyses will be performed separately for C-Tb and PPD. Response cut-offs will be used and only subjects with positive response will be included in the analyses. A linear, curvilinear or stepwise relationship will be used depending on the observed data. The SAP will state the final choice of cut-offs.

    A possible relationship between induration response and CD4 counts in the HIV positive sub-group will be evaluated as for the age above.


  • All adverse events occurring within 28 days after intradermal administration of C-Tb and PPD [ Time Frame: Onset between the injections and 28 days after the injections ] [ Designated as safety issue: Yes ]
    All adverse events occurring within 28 days after intradermal administration of C-Tb and Tuberculin PPD RT23 SSI will be tabulated descriptively.

  • Laboratory safety parameters: hematology, biochemistry and urinalysis in participants ≥ 5 years of age [ Time Frame: Onset between the injections and 28 days after the injections ] [ Designated as safety issue: Yes ]
    Laboratory safety parameters: hematology and biochemistry in participants ≥ 5 years of age will be tabulated descriptively and presented in shift tables.

  • Injection site adverse reactions within 2 to 3 days after intradermal administration of C-Tb and PPD [ Time Frame: Onset between the injections and 28 days after the injections ] [ Designated as safety issue: Yes ]
    The incidence of injection site adverse reactions within 2 to 3 days after intradermal administration will be compared between C-Tb and Tuberculin PPD RT23 SSI and the contrast will be presented with a confidence interval.


Estimated Enrollment: 1625
Study Start Date: September 2012
Estimated Primary Completion Date: October 2013 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: 0.1 µg/0.1 mL C-Tb
The C-Tb and 2 T.U. Tuberculin PPD RT 23 SSI agents are given concomitantly to each volunteer in the RIGHT and LEFT forearms according to a double blind randomisation scheme
Biological: C-Tb
The C-Tb agent is administered by the Mantoux injection technique to each volunteer in the RIGHT or LEFT forearm according to a double blind randomisation scheme
Active Comparator: 2 T.U. Tuberculin PPD RT 23 SSI
The C-Tb and 2 T.U. Tuberculin PPD RT 23 SSI agents are given concomitantly to each volunteer in the RIGHT and LEFT forearms according to a double blind randomisation scheme
Biological: 2 T.U. Tuberculin PPD RT 23 SSI
The 2 T.U. Tuberculin PPD RT 23 SSI agent is administered by the Mantoux injection technique to each volunteer in the RIGHT or LEFT forearm according to a double blind randomisation scheme

Detailed Description:

The TESEC-05 trial is an open comparison of the diagnostics performance of C-Tb compared to the QuantiFERON®-TB Gold In-Tube, in combination with a double-blind randomized split-body safety assessment of C-Tb versus to 2 T.U. Tuberculin PPD RT23 SSI.

The trial is a multi-centre Phase III clinical trial designed specifically to address C-Tb in relation to the paediatric population and to HIV infection. The intention is to evaluate how the C-Tb test performs in the paediatric population with respect to safety, and to ensure that SSI will be able to extrapolate data obtained in an adult population to the paediatric population.

Furthermore, the intention is both to evaluate the diagnostic performance and safety of C-Tb in HIV infected individuals and to evaluate whether SSI will be able to extrapolate data obtained in a non-HIV population to a HIV population.

The trial population will consist of paediatric participants with suspected TB infection and adult participants suspected to have TB disease. Furthermore a control group of 100 children between 5 - 11 years of age with no symptoms or known exposure will be recruited from an area with a "low" prevalence of TB (an area with an incidence rate < 299/100,000 per year, the average rate of TB in South Africa in 2005 was 645/100,000 per year.

The trial will be conducted in South Africa where the prevalence of HIV infection is high and MTb infections are endemic.

BCG vaccination at birth has been common practice since 1961 in South Africa. Thus most of the participants are presumed BCG vaccinated.

  Eligibility

Ages Eligible for Study:   up to 65 Years
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   Yes
Criteria

Inclusion Criteria:

HIV NEGATIVE PARTICIPANTS:

  1. Participants between 5 and 65 years attending the TB clinic due to suspicion of TB disease
  2. Infants, toddlers and children between 28 days and 4 years must either have symptoms or signs of TB or be in close contact to a smear positive pulmonary TB case (more than 6 hours/day)
  3. Is between 28 days and 65 years of age
  4. Participant, parent or legal guardian has signed the informed consent
  5. Is HIV negative confirmed by two rapid tests
  6. Is willing and likely to comply with the trial procedures
  7. Is prepared to grant authorized persons access to their medical record

HIV POSITIVE PARTICIPANTS:

  1. Participants between 5 and 65 years attending the TB clinic due to suspicion of TB disease
  2. Infants, toddlers and children between 28 days and 4 years must either have symptoms* or signs** of TB or be in close contact to a smear positive pulmonary TB case (more than 6 hours/day)
  3. Is between 28 days and 65 years of age
  4. Participant, parent or legal guardian has signed the informed consent
  5. Is HIV positive confirmed by:

    1. two positive rapid tests or
    2. 1 positive rapid test and an additional confirmatory ELISA test
  6. A CD4 count has been done
  7. Is willing and likely to comply with the trial procedures
  8. Is prepared to grant authorized persons access to their medical record

HIV NEGATIVE CONTROL GROUP:

  1. Participant with no known contact to people infected with MTb and no signs or symptoms of TB.
  2. Is between 5 and 11 years of age
  3. Participant, parent or legal guardian has signed the informed consent
  4. Is HIV negative confirmed by two rapid tests
  5. Is willing and likely to comply with the trial procedures
  6. Is prepared to grant authorized persons access to their medical record

Exclusion Criteria:

HIV NEGATIVE PARTICIPANTS:

  1. Has a confirmed diagnosis of tuberculosis at Screening Visit
  2. Has been vaccinated with a live vaccine within 6 weeks prior to the day of inclusion (e.g. MMR, yellow fever, oral typhoid vaccines) except BCG vaccine
  3. Has been tuberculin (TST) tested less than 12 months prior to the day of inclusion
  4. Is pregnant, breastfeeding or intending to get pregnant during the trial period
  5. Is a female of child bearing potential (12 years of age or older) not willing to use effective barrier (including spermicidal gel), hormonal or intrauterine contraceptive measures during the trial period
  6. Has an active disease affecting the lymphoid organs (e.g., Hodgkin's disease, lymphoma, leukaemia, sarcoidosis)
  7. Has a current skin condition which interferes with the reading of the C-Tb and PPD e.g. tattoos, severe scarring, burns/sunburns, rash, eczema, psoriasis, or any other skin disease at or near the injection sites
  8. Has a condition where blood drawings pose more than minimal risk for the participant, such as haemophilia, other coagulation disorders or significantly impaired venous access
  9. Currently participating in another clinical trial with an investigational or non-investigational drug or device or has participated in another clinical trial within the 3 months prior to dosing
  10. Has participated in previous clinical trials investigating the ESAT-6 and/or CFP-10 antigens
  11. Has a condition which in the opinion of the investigator is not suitable for participation in the trial

HIV POSITIVE PARTICIPANTS:

  1. Has a confirmed diagnosis of tuberculosis at Screening Visit
  2. Has been vaccinated with a live vaccine within 6 weeks prior to the day of inclusion (e.g. MMR, yellow fever, oral typhoid vaccines)
  3. Has been tuberculin (TST) tested less than 12 months prior to the day of inclusion
  4. Is pregnant, breastfeeding or intending to get pregnant during the trial period
  5. Is a female of child bearing potential (12 years of age or older) not willing to use effective barrier (including spermicidal gel), hormonal or intrauterine contraceptive measures during the trial period
  6. Has an active disease affecting the lymphoid organs except for HIV (e.g., Hodgkin's disease, lymphoma, leukaemia, sarcoidosis)
  7. Has a known diagnosis of AIDS or is receiving antiviral therapy at the time of Screening Visit
  8. Has a current skin condition which interferes with the reading of the C-Tb and PPD e.g. tattoos, severe scarring, burns/sunburns, rash, eczema, psoriasis, or any other skin disease at or near the injection sites
  9. Has a condition where blood drawings pose more than minimal risk for the participant, such as haemophilia, other coagulation disorders or significantly impaired venous access
  10. Currently participating in another clinical trial with an investigational or non-investigational drug or device or has participated in another clinical trial within the 3 months prior to dosing
  11. Has participated in previous clinical trials investigating the ESAT-6 and/or CFP-10 antigens
  12. Has a condition which in the opinion of the investigator is not suitable for participation in the trial

HIV NEGATIVE CONTROL GROUP:

  1. Has been vaccinated with a live vaccine within 6 weeks prior to the day of inclusion (e.g. MMR, yellow fever, oral typhoid vaccines) except BCG vaccine
  2. Has been tuberculin (TST) tested less than 12 months prior to the day of inclusion
  3. Has an active disease affecting the lymphoid organs (e.g., Hodgkin's disease, lymphoma, leukaemia, sarcoidosis)
  4. Has a current skin condition which interferes with the reading of the C-Tb and PPD e.g. tattoos, severe scarring, burns/sunburns, rash, eczema, psoriasis, or any other skin disease at or near the injection sites
  5. Has a condition where blood drawings pose more than minimal risk for the participant, such as haemophilia, other coagulation disorders, or significantly impaired venous access
  6. Currently participating in another clinical trial with an investigational or non-investigational drug or device, or has participated in another clinical trial within the 3 months prior to dosing
  7. Has participated in previous clinical trials investigating the ESAT-6 and/or CFP-10 antigens
  8. Has a condition which in the opinion of the investigator is not suitable for participation in the trial
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01642888

Contacts
Contact: Bettine Borregaard, RN +45 3268 3416 BTG@ssi.dk
Contact: Erik Carp, M.Sc. +45 3268 8657 ECA@ssi.dk

Locations
South Africa
Primecure Medicentre, Mercantile Hospital Recruiting
Port Elizabeth, Eastern Cape, South Africa, 6014
Contact: M. Gani, MD     + 27 (0) 41 404 0589     mashra@gctrials.co.za    
Principal Investigator: M. Gani, MD            
Worthwhile Clinical Trials, Lakeview Hospital Recruiting
Benoni 1501, Gauteng, South Africa, 1501
Contact: I. Mitha, MD     + 27 (0) 11 422 1928     drmitha@iafrica.com    
Principal Investigator: I. Mitha, MD            
Synexus Stanza Bopape Clinic Recruiting
Pretoria, Gauteng, South Africa, 0122
Contact: Boitumelo Sebopa, MD     + 27 (0) 12 812 0469     SBCRInv1@synexus-sa.co.za    
Principal Investigator: Boitumelo Sebopa, MD            
Setshaba Research Centre Recruiting
Pretoria, Gauteng, South Africa, 0152
Contact: M. Malahleha, MD     + 27 (0) 12 799 2422     mookho@setshaba.org.za    
Principal Investigator: M. Malahleha, MD            
Synnyside Medi-Clinic Not yet recruiting
Pretoria, Gauteng, South Africa, 0002
Contact: M. Fulat, MD     +27 (0)12 440 1768     fulat@gctrials.co.za    
Principal Investigator: M. Fulat, MD            
M2 Karl Bremer Hospital Recruiting
Bellville, Cape Town, Western Cape, South Africa, 7530
Contact: Andreas Diacon, MD     + 27 (0) 21 949 7751     ahd@sun.ac.za    
Principal Investigator: Andreas Diacon, MD            
Tiervlei Trial Centre, Karl Bremer Hospital Recruiting
Bellville, Cape Town, Western Cape, South Africa, 7530
Contact: Haylene Nell, MD     + 27 (0) 21 957 9400     haylenenell@ttctrials.co.za    
Principal Investigator: Haylene Nell, MD            
UCT Lung Institute, Groote Schuur Hospital Recruiting
Cape Town, Western Cape, South Africa, 7925
Contact: Keertan Dheda, MD     + 27 (0) 21 404 7650     keertan.dheda@uct.ac.za    
Principal Investigator: Keertan Dheda, MD            
Be Part Yoluntu Centre Recruiting
Paarl, Western Cape, South Africa, 7626
Contact: Lize Hellstrom, MD     + 27 (0) 21 868 3990     boylouw@mweb.co.za    
Principal Investigator: Lize Hellstrom, MD            
Sponsors and Collaborators
Statens Serum Institut
Investigators
Principal Investigator: Andreas Diacon, MD M2 Karl Bremer Hospital
Study Chair: Henrik Aggerbeck, M.Sc. Statens Serum Institut
  More Information

No publications provided

Responsible Party: Statens Serum Institut
ClinicalTrials.gov Identifier: NCT01642888     History of Changes
Other Study ID Numbers: TESEC-05, 2011-005078-40
Study First Received: July 5, 2012
Last Updated: January 18, 2013
Health Authority: European Union: European Medicines Agency

Additional relevant MeSH terms:
Tuberculosis
Mycobacterium Infections
Actinomycetales Infections
Gram-Positive Bacterial Infections
Bacterial Infections

ClinicalTrials.gov processed this record on May 19, 2013