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A Phase 2 Study to Evaluate the Dose and Pharmacodynamic Efficacy of Sialic Acid-Extended Release (SA-ER) Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy
This study is currently recruiting participants.
Study NCT01517880   Information provided by Ultragenyx Pharmaceutical Inc
First Received: January 17, 2012   Last Updated: May 21, 2012   History of Changes

No Study Results Posted on ClinicalTrials.gov for this Study
About Study Results Reporting on ClinicalTrials.gov
  Study Status: This study is currently recruiting participants.
  Estimated Study Completion Date: August 2013
  Estimated Primary Completion Date: June 2013 (Final data collection date for primary outcome measure)