Accuracy Testing of the Chromosomal Aberration and Gene Mutation Markers of the AMLProfiler

This study is currently recruiting participants.
Verified August 2012 by Skyline Diagnostics BV
Sponsor:
Collaborator:
Skyline Diagnostics BV is the European based Sponsor/ Manufacturer and Myraqa, Inc is the US Sponsor.
Information provided by (Responsible Party):
Skyline Diagnostics BV
ClinicalTrials.gov Identifier:
NCT01463410
First received: October 28, 2011
Last updated: August 29, 2012
Last verified: August 2012
  Purpose

This clinical study will demonstrate the accuracy of the chromosomal aberration and gene mutation markers of the AMLProfiler molecular diagnostic assay and generate clinical performance data to support a Pre-Market Approval (PMA) submission to the Food and Drug Administration for in vitro diagnostic use within the United States of America.

The objective is to demonstrate the positive and negative percent agreement of each marker by comparing AMLProfiler results from multiple clinical participating sites with data generated using a laboratory developed bi-directional sequencing method generated at the molecular diagnostic reference lab.

The AMLProfiler assay is a qualitative in vitro diagnostic test for the detection of AML or APL specific chromosomal aberrations (specific recurrent translocations and inversions), as well as expression of specific genetic markers in RNA extracted from bone marrow aspirates of patients with Acute Myeloid Leukemia.


Condition
Acute Myeloid Leukemia (AML)
Acute Promyelocytic Leukemia (APL)
Refractory Anemia With Excess of Blasts (RAEB)

Study Type: Observational
Study Design: Observational Model: Case-Only
Official Title: Accuracy Testing of the Chromosomal Aberration and Gene Mutation Markers of the AMLProfiler

Resource links provided by NLM:


Further study details as provided by Skyline Diagnostics BV:

Primary Outcome Measures:
  • Acceptance Criteria [ Time Frame: Sample taken at initial visit with no follow up (Day 1) ] [ Designated as safety issue: No ]
    The acceptance criteria based on lower level of the 95% CI of the positive or negative percent agreement for all markers.


Biospecimen Retention:   Samples With DNA

RNA from bone marrow samples will be retained.


Estimated Enrollment: 545
Study Start Date: October 2011
Estimated Study Completion Date: November 2012
Estimated Primary Completion Date: October 2012 (Final data collection date for primary outcome measure)
  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Sampling Method:   Probability Sample
Study Population

Bone marrow samples will be used in the study only from AML,APL or RAEB subjects. Written informed consent by subjects will be obtained for use of their bone marrow samples in this study. Each site will follow their own bone marrow aspiration procedure.

Criteria

Inclusion Criteria:

  1. Subjects with a cytopathologically confirmed diagnosis of AML subjects with refractory anemia with excess of blasts (RAEB) according to the WHO 2008 classification
  2. ≥ 18 years
  3. Written informed consent

Exclusion Criteria:

  1. Subjects without a cytopathologically confirmed diagnosis of AML subjects with refractory anemia with excess of blasts (RAEB) according to the WHO 2008 classification
  2. < 18 years
  3. Without written informed consent
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01463410

Locations
United States, New York
Memorial Sloan Kettering Cancer Center Recruiting
New York, New York, United States, 10065
Contact: Martin Tallman, MD     212-639-3842     TallmanM@mskcc.org    
Principal Investigator: Martin Tallman, MD            
Sub-Investigator: Ross Levine, MD            
United States, Ohio
James Cancer Hospital Recruiting
Columbus, Ohio, United States, 43210
Contact: Janelle Solt     614-247-1944     janelle.solt@osumc.edu    
Principal Investigator: Guido Marcucci, MD            
Germany
University Hospital Ulm Recruiting
Ulm, Germany, 89081
Contact: Lars Bullinger, MD     +49 731 50045703     lars.bullinger@uniklinik-ulm.de    
Principal Investigator: Hartmut Doehner, MD            
Netherlands
Erasmus Medical Center Recruiting
Rotterdam, Netherlands, 3015 AA
Contact: Emelie Hacker     +31 010 7034546     e.hacker@erasmusmc.nl    
Principal Investigator: Bob Lowenberg, MD            
United Kingdom
Cardiff University Recruiting
Cardiff, Heath Park, United Kingdom, CF144XN
Contact: Amanda Gilkes     +44 29 20744522     gilkes@cardiff.ac.uk    
Principal Investigator: Alan Burnett, MD            
Sponsors and Collaborators
Skyline Diagnostics BV
Skyline Diagnostics BV is the European based Sponsor/ Manufacturer and Myraqa, Inc is the US Sponsor.
Investigators
Principal Investigator: Martin Tallman, MD Memorial Sloan-Kettering Cancer Center
Principal Investigator: Guido Marcucci, MD James Cancer Hospital
Principal Investigator: Alan Burnett, MD Cardiff University- School of Medicine
Principal Investigator: Hartmut Doehner, MD University Hospital Ulm
Principal Investigator: Bob Lowenberg, MD Erasmus Medical Center
  More Information

Additional Information:
Myraqa  This link exits the ClinicalTrials.gov site

No publications provided

Responsible Party: Skyline Diagnostics BV
ClinicalTrials.gov Identifier: NCT01463410     History of Changes
Other Study ID Numbers: PROT-015
Study First Received: October 28, 2011
Last Updated: August 29, 2012
Health Authority: United States: Institutional Review Board

Additional relevant MeSH terms:
Anemia
Anemia, Refractory
Anemia, Refractory, with Excess of Blasts
Chromosome Aberrations
Chromosome Disorders
Leukemia
Leukemia, Myeloid, Acute
Leukemia, Myeloid
Leukemia, Promyelocytic, Acute
Hematologic Diseases
Myelodysplastic Syndromes
Bone Marrow Diseases
Pathologic Processes
Congenital Abnormalities
Genetic Diseases, Inborn
Neoplasms by Histologic Type
Neoplasms

ClinicalTrials.gov processed this record on May 23, 2013