Oral N-acetylcysteine for the Treatment of Parkinson's Disease

This study is currently recruiting participants.
Verified January 2013 by University of Minnesota - Clinical and Translational Science Institute
Sponsor:
Information provided by (Responsible Party):
University of Minnesota - Clinical and Translational Science Institute
ClinicalTrials.gov Identifier:
NCT01427517
First received: August 30, 2011
Last updated: January 14, 2013
Last verified: January 2013
  Purpose

The investigators are interested in determining if the investigators are able to detect changes in brain chemistry using Magnetic Resonance Spectroscopy (MRS) in individuals with Parkinson's disease (PD) and those without neurological disorders (healthy controls) when they are given the antioxidant N-acetylcysteine (NAC). This study will combine information from a medical history, a physical examination and disease rating scales with results obtained using MRS brain scans and pharmacokinetic studies from blood samples. This research will require 1 visit that will require about 4 to 5 hours of time. During this study, participants will provide their medical history, be examined and undergo a rating scale for about one hour; the brain scan and pharmacokinetic studies will require 1.5-2 hours of time; in total the study will take about 4-5 hours.


Condition Intervention Phase
Parkinson's Disease
Drug: N-acetylcysteine
Phase 1

Study Type: Interventional
Study Design: Endpoint Classification: Pharmacokinetics/Dynamics Study
Intervention Model: Single Group Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: Oral N-acetylcysteine for the Treatment of Parkinson's Disease

Resource links provided by NLM:


Further study details as provided by University of Minnesota - Clinical and Translational Science Institute:

Primary Outcome Measures:
  • GSH levels in brain and peripheral circulation in all subjects post-NAC administration [ Time Frame: Visit 1 ] [ Designated as safety issue: No ]

Estimated Enrollment: 9
Study Start Date: July 2011
Estimated Study Completion Date: December 2013
Estimated Primary Completion Date: December 2013 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: NAC
single oral administration of NAC 75 mg/kg to 140 mg/kg
Drug: N-acetylcysteine
Single, oral administration of N-acetylcysteine 75 mg/kg to 140 mg/kg
Other Name: NAC

Detailed Description:

Oxidative stress is implicated in the pathogenesis of a number of neurodegenerative diseases such as Parkinson's disease (PD). Further, levels of glutathione (GSH), a prevalent endogenous antioxidant, are decreased in the postmortem substantia nigra (SN) of individuals with PD, indicating increased oxidative stress, although this has yet not been confirmed in vivo. Increases in intracellular oxidative stress have also been observed in primary fibroblast cultures obtained from patients with GD, where enzyme replacement therapy resulted in increases in total GSH. The hypothesis that oxidative stress plays a key role in the neurodegeneration associated with PD suggests that antioxidants may be useful in altering disease progression.

N-acetylcysteine (NAC) is a well-known antioxidant that is thought to act both as a free radical scavenger and as a cysteine donor for the synthesis of GSH. NAC may be beneficial in the treatment of PD. Magnetic resonance spectroscopy (MRS) methods may be able to determine if there are effects from NAC on central nervous system GSH levels. In addition, use of red blood cell (RBC) measurements of GSH, if correlated with brain concentrations, could serve as an easily measured biomarker to help characterize and monitor response to therapy. The investigators therefore propose to conduct a study of the effect of a single, oral dose of NAC on central (brain) measures of GSH and peripheral (RBC) measures of GSH in people with PD and healthy controls, through the use of simultaneous MRS techniques and pharmacokinetic studies. The investigators hypothesis and specific aims are as follows:

Hypothesis: RBC and brain GSH concentrations will increase following oral NAC administration in individuals with Parkinson's disease (PD) and control participants.

Specific Aims:

  1. Quantitate baseline plasma and red blood cell GSH concentrations in those with PD and controls; and characterize NAC and GSH pharmacokinetics after a single oral NAC administration.
  2. Quantitate brain GSH levels (as ascertained through MRS) in those with PD and controls at baseline and after a single oral NAC administration simultaneously with Aim 1.
  3. Construct a pharmacokinetic model to evaluate the relationship between peripheral (plasma and RBC) and central (brain) GSH measurements.
  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   Yes
Criteria

Inclusion Criteria:

  1. All participants must be 18 years or older.
  2. All enrollees must understand and cooperate with requirements of the study in the opinion of the investigators and must be able to provide written informed consent.
  3. Individuals with medically stable Parkinson's disease (in the opinion of the investigator).
  4. All participants must not have taken antioxidants coenzyme Q-10, vitamin C, or vitamin E for 3 weeks prior to the study.
  5. Absence of dementia in all subjects, as determined by pre-scanning cognitive assessment.
  6. Control subjects who are able to undergo MRS

Exclusion Criteria:

  1. Inability to undergo MRI scanning without sedation
  2. Medically unstable conditions in any group as determined by the investigators
  3. Pregnant or lactating or those women of child-bearing age that are not using acceptable forms of contraception
  4. Diagnosis of asthma that is presently being treated with ANY medication, or past history of asthma/bronchospasm resulting in an emergency room visit, hospitalization or treatment
  5. Unable to adhere to study protocol for whatever reason
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01427517

Contacts
Contact: Sarah Hilbert, MS 612-624-7745 cnru@umn.edu

Locations
United States, Minnesota
University of Minnesota Recruiting
Minneapolis, Minnesota, United States, 55455
Contact: Sarah Hilbert, MS     612-624-7745     cnru@umn.edu    
Principal Investigator: Paul Tuite, MD            
Principal Investigator: James Cloyd, PharmD            
Sponsors and Collaborators
University of Minnesota - Clinical and Translational Science Institute
  More Information

No publications provided

Responsible Party: University of Minnesota - Clinical and Translational Science Institute
ClinicalTrials.gov Identifier: NCT01427517     History of Changes
Other Study ID Numbers: NAC
Study First Received: August 30, 2011
Last Updated: January 14, 2013
Health Authority: United States: Institutional Review Board

Keywords provided by University of Minnesota - Clinical and Translational Science Institute:
Parkinson's disease
Control

Additional relevant MeSH terms:
Parkinson Disease
Parkinsonian Disorders
Basal Ganglia Diseases
Brain Diseases
Central Nervous System Diseases
Nervous System Diseases
Movement Disorders
Neurodegenerative Diseases
Acetylcysteine
N-monoacetylcystine
Antiviral Agents
Anti-Infective Agents
Therapeutic Uses
Pharmacologic Actions
Expectorants
Respiratory System Agents
Free Radical Scavengers
Antioxidants
Molecular Mechanisms of Pharmacological Action
Protective Agents
Physiological Effects of Drugs
Antidotes

ClinicalTrials.gov processed this record on June 17, 2013