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55 studies found for:    GBA

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21 Recruiting International Collaborative Gaucher Group (ICGG) Gaucher Registry
Conditions: Gaucher Disease;   Cerebroside Lipidosis Syndrome;   Glucocerebrosidase Deficiency Disease;   Glucosylceramide Beta-Glucosidase Deficiency Disease
Intervention:
22 Active, not recruiting A Study of the Efficacy and Safety of Eliglustat Tartrate (Genz-112638) in Type 1 Gaucher Patients
Conditions: Gaucher Disease, Type 1;   Cerebroside Lipidosis Syndrome;   Glucocerebrosidase Deficiency Disease;   Glucosylceramide Beta-Glucosidase Deficiency Disease;   Gaucher Disease, Non-Neuronopathic Form
Intervention: Drug: eliglustat tartrate
23 Completed Bone Response to Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention: Drug: CEREDASE™
24 Recruiting Positron Emission Tomography (PET) Imaging in People With Gaucher Mutations
Conditions: Glucocerebrosidase Mutations;   Gaucher Disease
Intervention:
25 Unknown † Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Condition: Gaucher's Disease
Intervention: Drug: glucocerebrosidase
26 Completed Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher Disease
Condition: Gaucher's Disease
Intervention: Genetic: human glucocerebrosidase gene into autologous peripheral blood stem cells
27 Recruiting Thrombocytopathy in Gaucher Disease Patients
Conditions: Gaucher Disease;   Thrombocytopathy
Intervention:
28 Completed Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells
Condition: Gaucher's Disease
Intervention: Genetic: human glucocerebrosidase cDNA
29 Completed Effects of Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention:
30 Enrolling by invitation A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
31 Recruiting Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease
Condition: Gaucher Disease, Type 3
Intervention: Biological: velaglucerase alfa
32 Completed Study of Velaglucerase Alfa Enzyme Replacement Therapy in Japanese Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Biological: velaglucerase alfa
33 Completed Open-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT)
Condition: Gaucher Disease, Type 1
Intervention: Drug: GA-GCB
34 Recruiting Detecting Dopaminergic Deficits in Individuals At-risk for Parkinsonism
Conditions: Parkinson Disease;   Gaucher Disease;   Idiopathic Rapid Eye Movement Sleep Disorder
Intervention:
35 Enrolling by invitation Bariatric Surgery and Weight Loss on Energy Metabolism and Insulin Sensitivity
Conditions: Obesity;   Energy Expenditure;   Body Composition;   Insulin Sensitivity;   Response of Gastrointestinal Peptides
Interventions: Procedure: Laparoscopic Roux-en-Y gastric bypass;   Procedure: Laparoscopic gastric banding;   Procedure: Laparoscopic sleeve gastrectomy;   Behavioral: Low Calorie Diet
36 Completed Safety Study of AT2101 in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy
Condition: Gaucher Disease, Type 1
Intervention: Drug: AT2101
37 Recruiting Study to Determine Mutations in the Gaucher Gene in Patients With Idiopathic Parkinson's Disease for Phenotype-genotype Correlation
Conditions: Parkinson Disease;   Idiopathic Parkinson Disease
Intervention:
38 Completed The Effect of DBcare, a Food Supplement on Diabetes Control
Conditions: Diabetes Mellitus, Non-insulin Dependant;   Diabetes Mellitus Type 2;   Diabetes Mellitus, on Oral Hypoglycemic Treatment;   Adult Type Diabetes Mellitus
Intervention: Dietary Supplement: DBCARE
39 Completed OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: OGT 918
40 Completed A Safety and Efficacy Study of Two Dose Levels of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: Taliglucerase alfa
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† Indicates status has not been verified in more than two years