Now Available for Public Comment: Notice of Proposed Rulemaking (NPRM) for FDAAA 801 and NIH Draft Reporting Policy for NIH-Funded Trials
2 studies found for:    GLYCOGEN STORAGE DISEASE IV
Show Display Options
Rank Status Study
1 Active, not recruiting Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease
Conditions: Adult Polyglucoson Body Disease;   Glycogen Brancher Enzyme Deficiency;   Glycogen Storage Disease Type IV
Interventions: Drug: Triheptanoin;   Dietary Supplement: Vegetable Oil
2 Recruiting Pharmacokinetics of Alglucosidase Alfa in Patients Aged 8-18 Years of Age
Conditions: Pompe Disease (Late-Onset);   Glycogen Storage Disease Type II (GSD II);   Glycogenesis 2;   Acid Maltase Deficiency
Intervention: Biological: alglucosidase alfa

Indicates status has not been verified in more than two years