42 studies found for:    "Spinal muscular atrophy"
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Rank Status Study
21 Completed A Trial of Hydroxyurea in Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention: Drug: Hydroxyurea
22 Not yet recruiting Valproate and Levocarnitine in Children With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Interventions: Drug: Valproate, Levocarnitine;   Drug: Placebo
23 Completed Evaluation of the Muscle Strength and Motor Ability in Children With Spinal Muscle Atrophy(SMA) Treated With Valproic Acid
Condition: Spinal Muscular Atrophy
Intervention:
24 Unknown  Motor Development and Orthoses in Spinal Muscular Atrophy (SMA)
Condition: Spinal Muscular Atrophy
Intervention:
25 Completed Measuring Levels of SMN in Blood Samples of SMA Patients
Condition: Spinal Muscular Atrophy
Intervention:
26 Completed Phase II Study of Leuprolide and Testosterone for Men With Kennedy's Disease or Other Motor Neuron Disease
Conditions: Spinal Muscular Atrophy;   Amyotrophic Lateral Sclerosis;   Spinobulbar Muscular Atrophy
Interventions: Drug: leuprolide;   Drug: testosterone
27 Recruiting SMN Copy Number Distribution in Mali, West Africa
Condition: Spinal Muscular Atrophy
Intervention:
28 Unknown  Establishing Novel Detection Techniques for Various Genetic-Related Diseases by Applying DHPLC Platform.
Conditions: Spinal Muscular Atrophy;   Neonatal Hyperbilirubinemia;   Colon Cancer
Intervention:
29 Unknown  Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System
Condition: Spinal Muscular Atrophy
Intervention:
30 Recruiting Multi-disease Carrier Screening Test Validation
Conditions: Spinal Muscular Atrophy (SMA);   Carrier Screening;   Genetic Testing
Intervention: Procedure: Blood draw
31 Completed A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
32 Unknown  A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
33 Active, not recruiting
Has Results
Progressive Strength Training in Spinal Muscular Atrophy
Condition: Muscular Atrophy, Spinal
Intervention: Other: Progressive strength training
34 Recruiting Flu Vaccine Study in Neuromuscular Patients 2011
Conditions: Duchenne Muscular Dystrophy;   Spinal Muscular Atrophy;   Congenital Muscular Dystrophy
Intervention: Biological: 2011-2012 seasonal flu vaccine
35 Active, not recruiting Effects of Power Mobility on Young Children With Severe Motor Impairments
Conditions: Cerebral Palsy;   Arthrogryposis;   Spinal Muscular Atrophy;   Other Central Nervous System or Musculoskeletal Disorders
Interventions: Other: Power mobility;   Other: No intervention
36 Recruiting Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients
Condition: Spinal Muscular Atrophy
Interventions: Drug: 4-aminopyridine (dalfampridine, Ampyra);   Drug: Placebo
37 Completed Pilot Study of Growth Hormon to Treat SMA Typ II and III
Condition: Muscular Atrophy, Spinal
Interventions: Drug: somatotropin;   Drug: Placebo
38 Completed Levetiracetam for Cramps, Spasticity and Neuroprotection in Motor Neuron Disease
Conditions: Motor Neuron Disease;   Amyotrophic Lateral Sclerosis;   Primary Lateral Sclerosis;   Progressive Muscular Atrophy
Intervention: Biological: Levetiracetam
39 Completed Study to Evaluate the Efficacy of Riluzole in Children and Young Adults With Spinal Muscular Atrophy (SMA)
Condition: SMA
Intervention: Drug: Riluzole
40 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:

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Indicates status has not been verified in more than two years