3 studies found for:    "Pachyonychia congenita"
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Rank Status Study
1 Completed Study of TD101, a Small Interfering RNA (siRNA) Designed for Treatment of Pachyonychia Congenita
Condition: Pachyonychia Congenita
Interventions: Drug: TD101;   Drug: Normal saline (placebo)
2 Not yet recruiting Simvastatin Treatment of Pachyonychia Congenita
Condition: Pachyonychia Congenita
Intervention: Drug: Simvastatine
3 Unknown  Botulinumtoxin A Treatment in Epidermolysis Bullosa Simplex and Pachyonychia Congenita
Condition: Epidermolysis Bullosa Simplex
Interventions: Drug: Dysport® (Botulinumtoxin A (Btx A));   Drug: Placebo

Indicates status has not been verified in more than two years