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6 studies found for:    "Gaucher disease type 3"
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Rank Status Study
1 Completed OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease
Condition: Gaucher Disease
Intervention: Drug: OGT 918
2 Active, not recruiting Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease
Condition: Gaucher Disease, Type 3
Intervention: Biological: velaglucerase alfa
3 Completed Effects of Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
Intervention:
4 Completed PEG-Glucocerebrosidase for the Treatment of Gaucher Disease
Condition: Gaucher's Disease
Intervention: Drug: Lysodase
5 Completed Convection-Enhanced Delivery of Glucocerebrosidase to Treat Type 2 Gaucher Disease
Condition: Type 2 Gaucher Disease
Intervention:
6 Completed Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease
Condition: Gaucher Disease
Intervention: Procedure: Blood sample

Indicates status has not been verified in more than two years