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3 studies found for:    "Focal dermal hypoplasia"
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Rank Status Study
1 Recruiting Study of Selected X-linked Disorders: Goltz Syndrome
Conditions: Focal Dermal Hypoplasia (FDH);   Goltz Syndrome;   X Linked Disorders
Intervention:
2 Completed A Trial to Evaluate the Safety, Local Tolerability, Pharmacokinetics and Pharmacodynamics of LDE225 on Skin Basal Cell Carcinomas in Gorlin Syndrome Patients
Condition: Treatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome Patients
Interventions: Drug: Placebo;   Drug: LDE225;   Drug: LDE225 0.25%;   Drug: LDE225 0.75%
3 Completed Efficacy, Safety and Pharmacokinetics of Oral LDE225 in Treatment of Patients With Nevoid Basal Cell Carcinoma Syndrome
Conditions: Basal Cell Carcinoma;   Gorlin Syndrome;   Nevoid Basal Cell Carcinoma Syndrome
Interventions: Drug: LDE225;   Drug: Placebo

Indicates status has not been verified in more than two years